Scientists explore early life factors contributing to SMA
Spinal muscular atrophy (SMA) is a severe neurological disease for which there is presently no cure, although current therapies can ...
Tag: Spinal Muscular Atrophy
Discovery of a fundamental biological mechanism opens path for novel therapies
The lab of Yongchao C. Ma, PhD, at Stanley Manne Children's Research Institute at Ann & Robert H. Lurie Children's ...
A bitter battle over the ‘orphan drug’ program leaves patients’ pocketbooks at risk
A prescription drug that helps Lore Wilkinson walk and talk despite a rare muscle disease cost her so little for ...
Scientists explore links between survival motor neuron protein and sarcopenia
Adopting some of the strategies behind successfully treating the childhood disease spinal muscular atrophy may enable development of therapies to ...
